On a hospital bed, surrounded by white walls, beneath fluorescent lights, and a hum of medical machinery, filmmaker and comedian Jared “J.” Snow lifted his phone and pressed record. Hooked to an array ...

The first gene therapies approved to treat sickle cell disease in December 2023 are struggling on the market. But there are glimpses of forward momentum as Vertex and Genetix Bio provide updates.

Right now, approximately 20 billion red blood cells are busy traveling through your blood vessels. They are delivering oxygen to all the different tissues in your body and removing carbon dioxide to ...

Tatyana Thompson was diagnosed with sickle cell anemia as a baby. When she became a parent, her symptoms worsened. A treatment at Johns Hopkins finally cured her.

CRISPR gene therapy Casgevy can nearly eliminate sickle cell crises, but difficult stem‑cell collection is delaying access ...

Recent therapies like hydroxyurea (Droxia, Bristol-Myers Squibb), the first FDA-approved drug for SCD in 1994, increase fetal hemoglobin (HbF), which, through unknown pathways, improves SCD symptoms ...

This article is part of a Rare Disease series sponsored by DeepIntent. With Rare Disease Month wrapping up and Rare Disease Day taking place on Saturday, MM+M is celebrating a handful of campaigns ...

GREENVILLE, N.C. (WNCT) — WNCT’s Erin Jenkins sits down with a sickle cell disease survivor and a doctor to learn more about how far their research has come. Sickle cell disease is an inherited blood ...

As Uganda rolls out mandatory nationwide screening of newborns for sickle cell disease this month, a gene therapy celebrated ...

Regulators on Friday approved two new gene therapies for sickle cell disease that doctors hope can cure the painful, inherited blood disorder that afflicts mostly Black people in the United States.

Sickle cell anemia (SCA) is an inherited disorder of red blood cells. Some parents may learn that their infant has this disorder after prenatal testing. Hospitals also test for SCA after birth as part ...

An Alberta father is advocating for a legislation that would create national policies for fighting against sickle cell disease after his son died nearly four years ago. Jacob Marfo, director of Ezra ...